Dear Hardison & Cochran,
The MDA Office Team is so grateful for everything you have done for our families this year. You have sponsored our newsletter, Camp T-shirt and Gala; answered phones at the Jerry Lewis Labor Day Telethon; participated in Stride ‘n Ride and attended the Picnic; you have even locked-up a co-worker or two. And you have lifted our office morale with pizza and breakfast deliveries during our most demanding month!
MDA was established in 1950 as a partnership between scientists and concerned citizens with the desire to find a cure for the neuromuscular diseases that affect more than a million Americans. In this spirit, the MDA supports more research on neuromuscular diseases than any other private-sector organization in the world. The goal that was established nearly 60 years ago is becoming more of a reality each and every day, thanks to the support of people and companies like Hardison & Cochran.
Some of the most exciting breakthroughs are for the most common fatal genetic disorder called Duchenne Muscular Dystrophy. Because the Duchenne gene is carried on the X-chromosome, it primarily affects boys. It can happen to any family with about 30% of boys diagnosed having a new gene mutation (where the mother is not a carrier).
Ataluren, a brand name for the PTC-124 drug that has been tested for Duchenne MD, is in its “Pivotal” stage. This is the last stage that will be done with humans before they take the drug to FDA for approval. They expect that this drug will be on the market in early 2011…this drug will slow the progression of DMD for boys with nonsense mutation! This is about 15% of the boys with DMD that we serve. After steroids, this is the first real treatment option for our guys.
MDA helped to fund this research for an effective treatment—and now we can be the vehicle to make sure that every boy that can benefit from this drug will! But we need the continued support of our local community in order to make this happen.
So once again, the MDA Office would like to thank Hardison & Cochran for everything that you have done for us this year. This research, these treatments, and most of all, the hope that you have provided to our families through your support is priceless.
The Raleigh MDA Office
Marcy, Mary, Krissy, Laura, Maria, Kacey and Lauren